 The U.S. Food and Drug Administration (FDA) has granted orphan drug status to Gesynta Pharma’s GS-248, its oral therapy for people with systemic sclerosis (scleroderma). Orphan drug status aims to encourage therapies for rare diseases through benefits such as seven years of market exclusivity and exemption from FDA fees. “The orphan drug designation granted to our drug candidate GS-248
Dr Elizabeth Volkman, director of the UCLA Scleroderma Program, discusses gastrointestinal involvement in Systemic Sclerosis and how diet can affect your wellbeing.
Dr Elizabeth Volkmann talks us through some of the most common effects of gastrointestinal involvement in SSc: acid reflux, bloating, and diarrhoea - and details how to adapt your diet to improve these symptoms.
Dr. Price talks through some really useful information in the pre-recorded webinar above, including how to deal with dry eyes and antibodies that can indicate a vulnerability to scleroderma.
 Fat-derived cells from adults with diffuse cutaneous scleroderma that are then injected under the skin of the hands led to clinically meaningful improvements in hand function, according to published data from the Phase 3 STAR I clinical trial.
 Note: The headline of this story was updated April 19, 2022, to clarify that scleroderma isn’t becoming less rare, but rather awareness of the disease is increasing.
 This month’s Scleroderma Victoria Virtual Education Session topic is “Scleroderma and Intimacy”. Unfortunately due to unforeseen circumstances, the session was postponed and will be rescheduled soon. When we have a settled date, please join us as we hear from our guest speaker – a sex and relationship therapist – about adjustments you can make if necessary to ensure you and your partner feel fulfilled.
In the meantime, check out the Virtual Education Sessions to see what is on offer.  The main findings of scleroderma are thickening and tightening of the skin and inflammation and scarring of many body parts, leading to problems in the lungs, kidneys, heart, intestinal system, and other areas.
 Scleroderma symptoms can vary greatly from person to person, however, up to half of all scleroderma patients also develop lung problems.
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